Find-and-replace genome editing with CRISPR: A promising therapeutic strategy

Severe combined immunodeficiencies (SCIDs) are a group of debilitating primary immunodeficiency disorders, primarily caused by genetic mutations that disrupt T-cell development. SCID can also affect B-cell and natural killer cell function and counts. Left untreated, SCID proves fatal within the first year of life.

Leave A Comment

Your email address will not be published. Required fields are marked *