New method used to develop RNA therapy for the treatment of rare diseases

Having a rare genetic disease is actually pretty common. Rare diseases affect approximately 1 in 10 individuals, and more than 30 million people in the U.S. have a rare disease diagnosis. What makes them rare is that these 1 in 10 people affected have an estimated 7,000 different conditions, with treatments available for only about 5% of them.

Leave A Comment

Your email address will not be published. Required fields are marked *